Rare Diseases
Enabling new frontiers to transform the lives of patients with rare diseases
Data-driven patient insights enabling faster diagnosis and novel treatments to improve the quality of life of patients and their families
Enable breakthrough innovations to infuse hope intothe lives of rare disease patients
I too have dreams.
I want to be someone.
I want to go on to live a very full and rewarding life.
– From a Rare Disease Patient
More than 350 million people are affected by one of the 7,000+ rare diseases, with less than 5% having an approved treatment available. This huge unmet need in care and a commitment by manufacturers and regulators have instilled a sense of urgency to spur new scientific frontiers to transform the lives of patients with rare diseases.
The immense challenges associated with a rare disease, a consequence of a very small patient population, mean a delayed diagnostic process, difficult access to treatment and care, and high social, emotional, and financial burden on patients and their family.
Navigate these challenges and get commercialization support for rare disease treatments that create hope for patients, caregivers, and families.
Read Blog / Challenges Of Accelerating Diagnostic Journeys For Rare Diseases
We understand your commercial challenges
Raising physician awareness
Raising physician awareness
How to create awareness and education about rare diseases amongst healthcare professionals (HCPs)?
- Identify and maintain a targeted list of specialists
- Design and coordinate campaigns to create awareness about the disease across channels
- Perform marketing mix analysis specific to rare disease drugs
Supporting patients and caregivers
Supporting patients and caregivers
How to find, educate, and provide guidance and assistance to patients and caregivers?
- Design tactics to create awareness about drugs, and patient support services
- Perform marketing mix analysis
- Target parents and caregivers with frequent and personalized methods of engagement
Collaborating with advocacy groups
Collaborating with advocacy groups
How to establish trust with a dynamic community(advocacy groups) seeking help with a rare disease?
- Establish awareness and trust with advocacy groups by supporting them in their mission to help patients
- Leverage data-driven, multi-channel educational, and promotional programs and campaigns on the advocacy group’s channels (social and web)
Gaining market access
Gaining market access
What is the payer commercial value proposition (clinical and cost effectiveness)?
- Create a comprehensive and cohesive ‘value’ story for patients, providers, and payers
- Establish awareness and trust with payers to convey the benefits and differentiators of the drug prior to-and-post launch
- Use specialty pharmacies and limited distribution networks to exert greater control over pricing and use of specialty drugs
Our capabilities in rare disease
Sales analytics
- Commercial model design
- HCP and account-level segmentation
- Promotional response analysis
- Incentive plan design
- Territory alignment
- Call planning and targeting
Marketing analytics
- Launch planning
- ROI of marketing programs
- Digital engagement
- Marketing mix modeling
- Customer valuation
- Campaign management
Market access analytics
- Payer rebate reporting tools
- Specialty pharmacy performance
- IDN segmentation
- ROI analysis for managed markets tactics
- Pricing and contract analysis
Patient analytics
- Understanding treatment protocols and the patient journey
- Disease burden and cost of illness
- Patient compliance and persistence
- Drug utilization and patient profiling
Axtria research hub
White Paper
Axtria MarketingIQ™ as a Scalable Self-Service Alternative to Custom MMx Tools
Report
Novel Drug Approvals by the U.S. Food and Drug Administration in Rare Diseases: Findings From 2020–2023
Customer success stories
Case Study